Category GENE THERAPY RARE DISEASES

Atelerix Consortium Awarded £267,000 Innovate UK Grant for Collaboration with the Cell and Gene Therapy Catapult and Rexgenero on Cell Therapy Stabilisation Technologies

 Rexgenero, a regenerative medicine company pioneering the development of advanced cell-based therapies to treat chronic limb-threatening ischaemia (CLI), welcomes the news announced today by Atelerix that it has been awarded a grant of £267,000 from Innovate UK. The grant will be used to develop gel stabilisation technologies, developed by Atelerix, with the first objective of extending the

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New Articles in The CRISPR Journal

The CRISPR Journal announces the publication of its August 2019 issue. The Journal is dedicated to validating and publishing outstanding research and commentary on all aspects of CRISPR and gene editing, including CRISPR biology, technology, and genome editing, and commentary and debate of key policy, regulatory, and ethical issues affecting the field. The Journal, led by

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South Korea to revise bill to enable gene therapy research using gene editing

South Korea is seeking to ease legislative restrictions to allow research on breakthrough gene therapies using gene editing and other advanced gene correction tools. The Ministry of Health and Welfare said on Thursday it is revising the Bioethics Act to allow gene therapy research in this direction.  Rep. Yoon Il-kyu of the ruling Democratic Party,

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Pfizer invests half billion dollars to advance state-of-the-art gene therapy facility in Sanford, North Carolina

Pfizer announced today an additional half billion dollar investment for the construction of its state-of-the-art gene therapy manufacturing facility in Sanford, North Carolina. This facility is anticipated to support Pfizer’s continuing investment in gene therapy research and development, similar to Pfizer’s Chapel Hill and Kit Creek, North Carolina research and development sites. This facility would

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Gene Therapy Market Research Explores The Key Success Factors And Business Opportunities Including Key Players Forecast Till 2026

Source Transparency Market Research Gene Therapy Market – Snapshot The global gene therapy market is expanding at an exponential pace due to promising therapeutic outcomes of gene therapy, high prevalence and rise in incidence of cancer, and large number of clinical research pipeline products. In terms of revenue, the market was valued at US$ 17.0

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Clinical Trials: Gene Therapy

Source Global Data Gene therapy involves the delivery of complex treatments to patients. In recent years, there have been several promising clinical trial results within this field targeting an array of inherited neurodegenerative disorders, genetic diseases, and various cancers. Approvals based on these clinical trials have consequently encouraged interest in gene therapy from both industry

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This Drug Will Save Children’s Lives. It Costs $2 Million. NYT Editorial board position

Safety, innovation and affordability need not be mutually exclusive goals for cutting-edge treatments. Source NYT Spinal muscular atrophy is a condition often fatal by age 2. Babies with the disorder have a rare genetic mutation that prevents the nervous system from controlling certain muscles. As they grow to be toddlers, these children struggle to move their limbs,

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