All posts by PIER MARIA FORNASARI

PIER MARIA FORNASARI
2022-12-28

Strengthening the European translational research ecosystem for advanced therapy medicinal products (ATMPs) for rare diseases. An open Horizon Europe Framework Program for consortia.

Single stage with dead-line 15 march 2023 ExpectedOutcome: Research and innovation (R&I) actions to be supported under this topic must work towards results that contribute to all the following expected outcomes. Scope: There are over 7 000 rare diseases resulting in 30 million patients1 in Europe with a rare disease. Globally more than 300 million patients2 are

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PIER MARIA FORNASARI
2022-12-28

Wafer-thin device has potential to transform the field of islet cell transplantation

Implantable platform provides prolonged treatment of Type 1 diabetes A quarter-sized device created at Houston Methodist could drastically alter the course of treatment for Type 1 diabetes, a chronic condition that impacts millions of Americans and does not have a cure. In a study published in the Dec. 26 issue of Nature Communications, a research team led

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No Comments InREGENERATIVE MEDICINE
PIER MARIA FORNASARI
2022-12-19

Global study presents first results on the longer-term effects of therapies for the treatment of critically ill patients with COVID-19

The world’s largest trial into the effect of multiple interventions for critically ill adults with COVID-19 on longer-term outcomes has released results from the 180-day (six month) follow-up of 4869 critically ill patients. Published today in The Journal of the American Medical Association (JAMA), the study is part of the ongoing Randomized Embedded Multifactorial Adaptive Platform

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PIER MARIA FORNASARI
2022-12-07

Liver cancer study encourages caution with certain gene therapies

A newly discovered link between protein misfolding and liver cancer could help improve gene therapy for hemophilia Research led by Randal J. Kaufman, Ph.D., has found that misfolded proteins in liver cells contribute to the development of liver cancer, shedding new light on the mysterious origins of one of the world’s deadliest diseases. The findings, published

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No Comments InGENE THERAPY RARE DISEASES
PIER MARIA FORNASARI
2022-12-07

New treatments for blood cancers, new hope for patients: a new STAT e-book on CAR-T cells

Blood cancers like multiple myeloma have long been considered incurable, but in the last decade, the development of precision immunotherapy treatments has offered patients months or even years of extended life. One such treatment, known as CAR-T cell therapy, turns immune system T cells into killers of cancer cells. They have been so transformative that

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PIER MARIA FORNASARI
2022-12-07

Efficacy and safety of COVID‐19 vaccines: a Cochrane Systematic Review

A comprehensive review of all the evidence available from randomized controlled trials of COVID 19 vaccines up to November 2021 has concluded that most protect against infection and severe or critical illness caused by the virus. The review, performed by a collaboration of independent, international experts, and published in Cochrane Library also found there was

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No Comments InCovid-19