Archives: 2020-03-06

Scientists at Oregon edit genes inside the body using CRISPR for a hereditary blindness disorder, in a trial called BRILLIANCE.

A person with a genetic condition that causes blindness has become the first to receive a CRISPR–Cas9 gene therapy administered directly into their body. The treatment is part of a landmark clinical trial to test the ability of CRISPR–Cas9 gene-editing techniques to remove mutations that cause a rare condition called Leber’s congenital amaurosis 10 (LCA10).

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Just Released: ARM’s 2019 Annual Report & Sector Year in Review

ARM today released its 2019 Annual Report and Sector Year in Review, highlighting the organization’s key priorities and initiatives, as well as offering an in-depth look at trends and metrics for the cell therapy, gene therapy, and tissue engineering sector. ARM, which celebrated its 10th anniversary in 2019, is the premier international advocacy organization representing the cell

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JAMA Drug Pricing Issue: Pharma’s Outsized Profits and Lobbying Spend

In a presidential election year where the high cost of prescription drugs has been a major campaign issue, JAMA joined the fray with a special issue on drug pricing. Source MEDPAGETODAY Four studies — three in JAMA and one in JAMA Internal Medicine — along with a handful of editorials dig deeper into key questions about the U.S. pharmaceutical industry: Is

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Covid-19: Chinese researchers say virus evolved in 2 types

The coronavirus has evolved into two major types, with differing transmission rates and geographical distribution, according to a study published in the National Science Review yesterday. A group of Chinese scientists analysed 103 coronavirus genomes and identified mutations in 149 sites across the strains. They found that one type, which they called the L type, was more

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